Biotech Firms Target Alpha-1 Antitrypsin Deficiency With Precision Gene Editing

By Jason Mast · STAT News · 2026-07-28

Biotech Firms Target Alpha-1 Antitrypsin Deficiency With Precision Gene Editing

According to STAT News, a wave of biotechnology companies including Beam Therapeutics and Wave Life Sciences is racing to develop curative treatments for a rare genetic liver and lung disorder. The surge in activity follows the realization that new technologies capable of alterin

According to STAT News, a wave of biotechnology companies including Beam Therapeutics and Wave Life Sciences is racing to develop curative treatments for a rare genetic liver and lung disorder. The surge in activity follows the realization that new technologies capable of alterin